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Chenodeoxycholic acid Leadiant (previously Chenodeoxycholic acid sigma-tau)
chenodeoxycholic acid
Xantomatose cerebrotendinosa; Erros inatos do metabolismo
✅ Autorizado
✅
Nenhum alerta ativo
Este medicamento não apresenta escassez contínua, cartas de segurança ou recolhimentos.
Para que serve
Chenodeoxycholic acid is indicated for the treatment of inborn errors of primary bile acid synthesis due to sterol 27 hydroxylase deficiency (presenting as cerebrotendinous xanthomatosis (CTX)) in infants, children and adolescents aged 1 month to 18 years and adults.
⚠️ Segurança do paciente
No
Página oficial da EMA
https://www.ema.europa.eu/en/medicines/human/EPAR/chenodeoxycholic-acid-leadiant