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Active substance
genetically modified autologous CD34+ cell enriched population that contains haematopoietic stem and progenitor cells (HSPC) transduced ex vivo using a lentiviral vector encoding the human Wiskott-Aldrich Syndrome (WAS) gene
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1 EU-authorised brand(s)
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All clear right now
No active EU-wide shortages or safety letters for this substance. National-level issues may still exist.