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Chenodeoxycholic acid Leadiant (previously Chenodeoxycholic acid sigma-tau)
chenodeoxycholic acid
Xantomatosi cerebrotendinea; Errori congeniti del metabolismo
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Autorizzato
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Nessun allarme attivo
Questo medicinale non presenta carenze in corso, lettere di sicurezza o richiami.
A cosa serve
Chenodeoxycholic acid is indicated for the treatment of inborn errors of primary bile acid synthesis due to sterol 27 hydroxylase deficiency (presenting as cerebrotendinous xanthomatosis (CTX)) in infants, children and adolescents aged 1 month to 18 years and adults.
โ ๏ธ Sicurezza del paziente
No
Pagina ufficiale EMA
https://www.ema.europa.eu/en/medicines/human/EPAR/chenodeoxycholic-acid-leadiant